For 62 years, NTSAD has been bringing together leaders in the rare disease community to share, learn, network, and collaborate with families, researchers, clinicians and friends. NTSAD’s annual Imagine & Believe is a vital part of this effort.
Through Imagine & Believe we:
Join us in honoring Dr. Cynthia Tifft, M.D., Ph.D., Deputy Clinical Director of the National Human Genome Research Institute/NIH. A trusted partner and advisor to NTSAD since 1998, Dr. Cynthia Tifft is an accomplished clinician and scientist, and an extraordinary advocate for the rare disease community. Always prioritizing the children and adults for whom she cares, Dr. Tifft has led an almost 20-year long natural history study for storage disorders laying essential groundwork for clinical trials. Dr. Tifft is the Principal Investigator for a newly opened GM1 gangliosidosis gene therapy clinical trial, a career milestone.